Asian Journal of Advances in Orphan Pharmacotherapy

Welcome to the Asian Journal of Advances in Orphan Pharmacotherapy (AJAOP) — a peer-reviewed, open-access journal dedicated to advancing research, clinical insights, and therapeutic innovation in the field of orphan drugs, rare disease treatments, and specialized pharmacotherapy.

AJAOP serves as a platform for healthcare professionals, pharmacologists, researchers, and policy makers to explore emerging trends, novel drug discoveries, regulatory frameworks, and patient-centered care models specifically targeting rare and neglected diseases. Our focus spans across the Asian continent, with a global outlook on breakthroughs and best practices in orphan pharmacotherapy.

Focus Areas Include:

• Development and clinical trials of orphan drugs
• Rare and ultra-rare disease pharmacotherapy
• Pharmacovigilance and safety monitoring in rare disease management
• Regulatory, policy, and pricing challenges in orphan drug approval
• Real-world evidence and patient outcomes
• Genetic and molecular therapies for rare conditions
• Global collaboration models and Asian regional advancements

Why AJAOP?

• Regionally Focused, Globally Relevant: Bridging the gap in research from Asia and promoting international collaborations.
• Rapid and Rigorous Review: Double-blind peer review ensures high-quality and timely publications.
• Open Access for All: Free to read, share, and download – supporting knowledge equity in orphan disease care.
• Interdisciplinary Dialogue: Bringing together academia, clinical practice, pharma industry, and policy discussions under one roof.

Recent Topics:

• Progress in gene therapies for rare metabolic disorders
• Access challenges in low-resource settings for orphan medications
• Pediatric orphan drug development strategies
• Pharmacoeconomic considerations for niche therapies in Asia

Call for Papers Open!

We invite researchers, clinicians, and policy experts to contribute original research, reviews, and case studies.